| trial_id,disease,phase,target_n,n_eligible,n_approached,n_consented,n_consent_refused,n_screened,n_screen_fail,n_screen_pass,n_enrolled,n_target_met,enrollment_rate,screen_fail_rate |
| TRIAL-GD-001,Gaucher Disease Type 1,Phase 3,120,72,72,48,24,48,12,36,29,0,0.403,0.25 |
| TRIAL-SMA-001,Spinal Muscular Atrophy,Phase 3,80,59,59,48,11,48,16,32,27,0,0.458,0.333 |
| TRIAL-CF-001,Cystic Fibrosis,Phase 3,200,164,164,114,50,114,44,70,57,0,0.348,0.386 |
| TRIAL-DMD-001,Duchenne Muscular Dystrophy,Phase 2/3,60,82,82,56,26,56,13,43,30,0,0.366,0.232 |
| TRIAL-HD-001,Huntington Disease,Phase 2/3,100,16,16,11,5,11,3,8,6,0,0.375,0.273 |
| TRIAL-FAB-001,Fabry Disease,Phase 3,90,38,38,28,10,28,12,16,11,0,0.289,0.429 |
| TRIAL-MFS-001,Marfan Syndrome,Phase 3,150,176,176,142,34,142,51,91,73,0,0.415,0.359 |
| TRIAL-HEM-001,Hemophilia A,Phase 3,70,35,35,28,7,28,7,21,18,0,0.514,0.25 |
| TRIAL-PKD-001,ADPKD,Phase 3,180,126,126,90,36,90,30,60,47,0,0.373,0.333 |
| TRIAL-OI-001,Osteogenesis Imperfecta,Phase 2/3,100,60,60,43,17,43,17,26,20,0,0.333,0.395 |
| TRIAL-TS-001,Tuberous Sclerosis,Phase 3,80,62,62,40,22,40,13,27,20,0,0.323,0.325 |
| TRIAL-SCD-001,Sickle Cell Disease,Phase 3,75,112,112,86,26,86,20,66,59,0,0.527,0.233 |
| TRIAL-NPC-001,Niemann-Pick Type C,Phase 2/3,50,49,49,37,12,37,12,25,21,0,0.429,0.324 |
| TRIAL-LCA-001,Leber Congenital Amaurosis,Phase 3,40,44,44,34,10,34,8,26,21,0,0.477,0.235 |
| TRIAL-CAH-001,Congenital Adrenal Hyperplasia,Phase 3,110,75,75,57,18,57,21,36,28,0,0.373,0.368 |
|
|